Circulation:“垃圾基因”并不是一无是处,它可以治疗心脏病

2017-08-29 佚名 生物探索

加州大学洛杉矶分校和霍华德休斯医学研究所的科学家近日发现,LeXis这个“垃圾DNA”,或许并不是一无是处,或许可以使用它来治疗心脏病。研究成果发表在《Circulation》杂志上。



加州大学洛杉矶分校和霍华德休斯医学研究所的科学家成功地使用了一种抑制胆固醇水平的基因作为一种治疗方法,目的是减少家族性高胆固醇血症引起的血小板增多。在临床预实验中,研究人员发现LeXis基因可降低胆固醇和减少动脉阻塞,而且这种治疗方法似乎还可以减少肝细胞中的脂肪堆积。该研究发表在《Circulation》杂志上。

家族性高胆固醇血症(FH)是一种遗传病,又称家族性高β脂蛋白血症。临床特点是高胆固醇血症、特征性黄色瘤、早发心血管疾病家族史。

LeXis基因属于一组独特的基因,一直被认为是“垃圾DNA”,因为科学家认为它们没有什么作用。然而,人类基因组计划的证据表明,LeXis等基因实际上是活跃的。这些基因被称为长链非编码RNA(lncRNAs),是生物学的研究热点之一。

研究人员想测试单次注射基因LeXis是否能减缓心脏病的发展。为此,他们给小鼠注了了“LeXis”,并设置对照组,然后给小鼠喂食了15周的高盐高胆固醇的食物——相当于快餐汉堡和炸薯条。随后研究人员测量了心脏病的进展。

尽管之前的研究已经表明IncRNAs很重要,但这是首次表明IncRNAs可以被用于基因治疗来治疗人类疾病。“垃圾基因”未来可能有助于治疗家族性高胆固醇血症和其他难以治疗的疾病。

他们下一步将在大型动物身上确认这一发现,并结合目前可用的治疗方法来测试这一疗法。

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    2017-08-30 flysky120

    学习一下知识

    0

  2. [GetPortalCommentsPageByObjectIdResponse(id=238660, encodeId=2b5f23866016, content=学习一下知识, beContent=null, objectType=article, channel=null, level=null, likeNumber=57, replyNumber=0, topicName=null, topicId=null, topicList=[], attachment=null, authenticateStatus=null, createdAvatar=http://cacheapi.medsci.cn/resource/upload/20160718/IMG578C993D395567540.jpg, createdBy=59b81918946, createdName=flysky120, createdTime=Wed Aug 30 11:55:33 CST 2017, time=2017-08-30, status=1, ipAttribution=), GetPortalCommentsPageByObjectIdResponse(id=238428, encodeId=e60723842891, content=很有趣的研究.学习了, beContent=null, objectType=article, channel=null, level=null, likeNumber=63, replyNumber=0, topicName=null, topicId=null, topicList=[], attachment=null, authenticateStatus=null, createdAvatar=, createdBy=e97e27354, createdName=lcm1028, createdTime=Tue Aug 29 21:12:01 CST 2017, time=2017-08-29, status=1, ipAttribution=), GetPortalCommentsPageByObjectIdResponse(id=238383, encodeId=bc15238383a0, content=很好!, beContent=null, objectType=article, channel=null, level=null, likeNumber=54, replyNumber=0, topicName=null, topicId=null, topicList=[], attachment=null, authenticateStatus=null, createdAvatar=http://cacheapi.medsci.cn/resource/upload/20160804/IMG57A2EF131ACE72300.jpg, createdBy=a2811610046, createdName=黄庆, createdTime=Tue Aug 29 17:34:54 CST 2017, time=2017-08-29, status=1, ipAttribution=), GetPortalCommentsPageByObjectIdResponse(id=238375, encodeId=aafe2383e576, content=不了解作用不等于没有作用, beContent=null, objectType=article, channel=null, level=null, likeNumber=53, replyNumber=0, topicName=null, topicId=null, topicList=[], attachment=null, authenticateStatus=null, createdAvatar=https://cdnapi.center.medsci.cn/medsci/head/2017/08/28/91007f8cecd75d97869cd5ac7ec78615.jpg, createdBy=b6121303678, createdName=lxf810720a, createdTime=Tue Aug 29 16:55:53 CST 2017, time=2017-08-29, status=1, ipAttribution=), GetPortalCommentsPageByObjectIdResponse(id=238373, encodeId=da862383e325, content=造物主制造的每一个成分都是有效的, beContent=null, objectType=article, channel=null, level=null, likeNumber=57, replyNumber=0, topicName=null, topicId=null, topicList=[], attachment=null, authenticateStatus=null, createdAvatar=https://wx.qlogo.cn/mmopen/ajNVdqHZLLCYbPBa7AiaIy1pMpp7CF9lHORw4icR9GOrMO6RVNCb1qSUSY9TFBzW5zlrpDia0HKafiarjvcweMaVdg/0, createdBy=f1d61928636, createdName=simayunhe, createdTime=Tue Aug 29 16:11:07 CST 2017, time=2017-08-29, status=1, ipAttribution=), GetPortalCommentsPageByObjectIdResponse(id=238324, encodeId=470e23832487, content=谢谢分享.学习受益匪浅, beContent=null, objectType=article, channel=null, level=null, likeNumber=18, replyNumber=0, topicName=null, topicId=null, topicList=[], attachment=null, authenticateStatus=null, createdAvatar=https://wx.qlogo.cn/mmopen/Q3auHgzwzM4o2XVpJ6449yqDsjibydI5HnJ8MibGxNn4HZiaZib0bdfibbwoz3KQrIyN9AGxq36ZlZRNicYlPfOOWMtwgsajY6mGNFiaPclFdowjD0/0, createdBy=97bd1338592, createdName=清风拂面, createdTime=Tue Aug 29 12:24:22 CST 2017, time=2017-08-29, status=1, ipAttribution=)]
    2017-08-29 lcm1028

    很有趣的研究.学习了

    0

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    2017-08-29 黄庆

    很好!

    0

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    2017-08-29 lxf810720a

    不了解作用不等于没有作用

    0

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    2017-08-29 simayunhe

    造物主制造的每一个成分都是有效的

    0

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    2017-08-29 清风拂面

    谢谢分享.学习受益匪浅

    0

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