Allele-Selective Suppression of Mutant Huntingtin in Primary Human Blood Cells

Miller, JRC; Pfister, EL; Liu, WZ; Andre, R; Traager, U; Kennington, LA; Lo, K; Dijkstra, S; Macdonald, D; Ostroff, G; Aronin, N; Tabrizi, SJ

Tabrizi, SJ (reprint author), UCL, Dept Neurodegenerat Dis, UCL Inst Neurol, London WC1N 3BG, England.

SCIENTIFIC REPORTS, 2017; 7 ( ):