Syngeneic AAV Pseudo-particles Potentiate Gene Transduction of AAV Vectors

Wang, QZ; Dong, BA; Pokiniewski, KA; Firrman, J; Wu, ZR; Chin, MPS; Chen, XW; Liu, LS; Xu, RA; Diao, Y; Xiao, WD

Diao, Y (reprint author), Huaqiao Univ, Sch Biomed Sci, Quanzhou 362021, Fujian, Peoples R China.; Xiao, WD (reprint author), Temple Univ, Sol Sherry Thrombosis Res Ctr, Philadelphia, PA 19122 USA.

MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, 2017; 4 ( ): 149

Abstract

Adeno-associated virus (AAV) vectors have emerged as a safe and efficient gene therapy platform. One complication is that a significant amount of empt......

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