CRISPR deletion of the C9ORF72 promoter in ALS/FTD patient motor neurons abolishes production of dipeptide repeat proteins and rescues neurodegeneration-MedSci.cn

CRISPR deletion of the C9ORF72 promoter in ALS/FTD patient motor neurons abolishes production of dipeptide repeat proteins and rescues neurodegeneration

Krishnan, G; Zhang, Y; Gu, YZ; Kankel, MW; Gao, FB; Almeida, S

Gao, FB; Almeida, S (corresponding author), Univ Massachusetts, Dept Neurol, Med Sch, Worcester, MA 01605 USA.