Clinical advances of siRNA therapeutics

Hu, B; Weng, YH; Xia, XH; Liang, XJ; Huang, YY

Huang, YY (reprint author), Beijing Inst Technol, Sch Life Sci, Adv Res Inst Multidisciplinary Sci, Key Lab Mol Med & Biotherapy, 5 Zhongguancun South St, Beijing 100081, Peoples R China.

JOURNAL OF GENE MEDICINE, 2019; 21 (7):

Abstract

Small interfering RNA (siRNA) enables efficient target gene silencing by employing a RNA interference (RNAi) mechanism, which can compromise gene expr......

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