Allele-selective lowering of mutant HTT protein by HTT-LC3 linker compounds

Li, ZY; Wang, C; Wang, ZY; Zhu, CG; Li, J; Sha, T; Ma, LX; Gao, C; Yang, Y; Sun, YM; Wang, J; Sun, XL; Lu, CQ; Difiglia, M; Mei, YN; Ding, C; Luo, SQ; Dang, YJ; Ding, Y; Fei, YY; Lu, BX

Ding, Y; Lu, BX (reprint author), Fudan Univ, Huashan Hosp, State Key Lab Med Neurobiol, Neurol Dept, Shanghai, Peoples R China.; Ding, Y; Lu, BX (reprint author), Fudan Univ, Sch Life Sci, Inst Brain Sci, MOE Frontiers Ctr Brain Sci, Shanghai, Peoples R

NATURE, 2019; 575 (7781): 203