Inotersen and severe thrombocytopenia: Two case reports and review

Senin, LD; Garro, CB; Gomez, ES; Santos-Rubio, MD

Senin, LD (通讯作者),Hosp Juan Ramon Jimenez, Serv Farm Hosp, Ronda Exterior Norte S N, Huelva 21005, Spain.

INTERNATIONAL JOURNAL OF CLINICAL PHARMACOLOGY AND THERAPEUTICS, 2022; 60 (7): 311

Abstract

Hereditary transthyretin amyloidosis (hATTR) is an ultra-rare illness. Inotersen is a 2???-O-methoxyethyl (2???MOE)modified antisense oligonucleotides......

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