An Overview of the Therapeutic Strategies for the Treatment of Spinal Muscular Atrophy

Li, YY; Zeng, HY; Wei, YH; Ma, XL; He, ZY

Ma, XL (通讯作者),Sichuan Univ, West China Hosp, Canc Ctr, Dept Biotherapy, 37 Guoxue Alley, Chengdu 610041, Peoples R China.;He, ZY (通讯作者),Sichuan Univ, West China Hosp, Dept Pharm, 37 Guoxue Alley, Chengdu 610041, Peoples R China.

HUMAN GENE THERAPY, 2023; 34 (5-6): 180

Abstract

Spinal muscular atrophy (SMA) is a recessive, neurodegenerative disorder. It is one of the most common genetic causes of infant mortality and is chara......

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