Long-term effects of ivacaftor on nonpulmonary outcomes in individuals with cystic fibrosis, heterozygous for a S1251N mutation

Burghard, M; Berkers, G; Ghijsen, S; Hollander-Kraaijeveld, FM; de Winter-de Groot, KM; van der Ent, CK; Heijerman, HGM; Takken, T; Hulzebos, HJ

Burghard, M (corresponding author), Wilhelmina Childrens Hosp, Child Dev & Exercise Ctr, Dept Pediat, POB 85090, NL-3508 EA Utrecht, Netherlands.

PEDIATRIC PULMONOLOGY, 2020; 55 (6): 1400

Abstract

Objectives To describe the long-term effects of ivacaftor (Kalydeco (R)) in individuals with cystic fibrosis (CF) on body mass index (BMI), body compo......

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