Curing SMA: Are we there yet?

Reilly, A; Chehade, L; Kothary, R

Kothary, R (通讯作者)，Ottawa Hosp Res Inst, Regenerat Med Program, Ottawa, ON, Canada.;Kothary, R (通讯作者)，Univ Ottawa, Ctr Neuromuscular Dis, Ottawa, ON, Canada.;Kothary, R (通讯作者)，Univ Ottawa, Dept Cellular & Mol Med, Ottawa, ON, Canada.;Kothary, R (通讯作者)，Univ Ottawa, Dept Biochem Microbiol & Immunol, Ottawa, ON, Canada.;Kothary, R (通讯作者)，Univ Ottawa, Dept Med, Ottawa, ON, Canada.

GENE THERAPY, 2023; 30 (1-2): 8

Abstract

Loss or deletion of survival motor neuron 1 gene (SMN1) is causative for a severe and devastating neuromuscular disease, Spinal Muscular Atrophy (SMA)......

Full Text Link


Links

期刊讨论 | 中国SCI论文 | 期刊主页 | 投稿经验 | 杂志官网 | 投稿链接 | 作者需知 | PMC链接 | Pubmed全文检索