The rapidly evolving state of gene therapy

Gruntman, AM; Flotte, TR

Flotte, TR (reprint author), Univ Massachusetts, Sch Med, Suite 340,55 Lake Ave North, Worcester, MA 01655 USA.

FASEB JOURNAL, 2018; 32 (4): 1733

Abstract

Gene therapy is emerging as a viable option for clinical therapy of monogenic disorders and other genetically defined diseases, with approved gene the......

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