EVOLUTION OF THE HGB-206 STUDY DESIGN FOR EVALUATING LENTIGLOBIN GENE THERAPY IN SICKLE CELL DISEASE

Chawla, A; Kanter, J; Mapara, M; Kwiatkowski, J; Krishnamurti, L; Schmidt, M; Miller, A; Pierciey, F; Shi, WL; Ribeil, JA; Asmal, M; Thompson, A; Walters, M; Tisdale, J

PEDIATRIC BLOOD & CANCER, 2019; 66 ():