Gene Augmentation of CHM Using Non-Viral Episomal Vectors in Models of Choroideremia

Toualbi, L; Toms, M; Almeida, PV; Harbottle, R; Moosajee, M

Moosajee, M (通讯作者)，UCL Inst Ophthalmol, Dev Ageing & Dis, London EC1V 9EL, England.;Moosajee, M (通讯作者)，Francis Crick Inst, Ocular Genom & Therapeut, London NW1 1AT, England.;Moosajee, M (通讯作者)，Moorfields Eye Hosp NHS Fdn Trust, Dept Genet, London EC1V 2PD, England.

INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, 2023; 24 (20):

Abstract

Choroideremia (CHM) is an X-linked chorioretinal dystrophy leading to progressive retinal degeneration that results in blindness by late adulthood. It......

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