FVIII-Expressing Human Placental Cells Engraft in Multiple Organs and Provide FVIII Protein While Evading Induction of FVIII Inhibitors When Administered to Juvenile Sheep

Trevisan, B; Rodriguez, M; Dizon, J; George, S; Shields, JE; Lankford, S; Combs, R; Owen, J; Atala, A; Doering, CB; Spencer, HT; Porada, C; Almeida-Porada, MG

MOLECULAR THERAPY, 2022; 30 (4): 581