Givosiran to treat acute porphyria

Honor, A; Rudnick, SR; Bonkovsky, HL

Honor, A (corresponding author), Wake Forest Baptist Med Ctr, Sect Gastroenterol, 1 Med Ctr Blvd, Winston Salem, NC 27157 USA.

DRUGS OF TODAY, 2021; 57 (1): 47

Abstract

Porphyrias are a family of rare diseases chiefly due to inborn errors of heme biosynthesis. The porphyrias are generally characterized either by the m......

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