Givosiran: First Approval

Scott, LJ

Scott, LJ (corresponding author), Springer Nat, Private Bag 65901, Auckland 0754, New Zealand.

DRUGS, 2020; 80 (3): 335

Abstract

Givosiran (Givlaari (TM)) is an aminolevulinate synthase 1 (ALAS1)-directed small interfering RNA (siRNA) covalently linked to a ligand to enable spec......

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