Risdiplam: A Review in Spinal Muscular Atrophy

Paik, J

Paik, J (通讯作者),Springer Nat, Mairangi Bay,Private Bag 65901, Auckland 0754, New Zealand.

CNS DRUGS, 2022; 36 (4): 401

Abstract

Plain Language Summary Patients with spinal muscular atrophy (SMA) have insufficient levels of survival motor neuron (SMN) protein due to a defect in ......

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