Risdiplam: First Approval

Dhillon, S

Dhillon, S (corresponding author), Springer Nat, Private Bag 65901, Auckland 0754, New Zealand.

DRUGS, 2020; 80 (17): 1853

Abstract

Risdiplam (Evrysdi (TM)) is an orally administered, survival motor neuron 2 (SMN2)-directed RNA splicing modifier being developed by Roche, PTC Therap......

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