UPDATE ON THE FIRST PATIENTS WITH SEVERE HEMOGLOBINOPATHIES TREATED WITH LENTIGLOBIN GENE THERAPY

Ribeil, JA; Hacein-Bey-Abina, S; Payen, E; Magrin, E; Magnani, A; Semeraro, M; Caccavelli, L; Touzot, F; Lefrere, F; Suarez, F; Hermine, O; Brousse, V; Poirot, C; Moshous, D; Bourget, P; El-Nemer, W; Bartolucci, P; Weber, L; Puy, H; Meritet, JF; Grev

HAEMATOLOGICA, 2017; 102 ( ): 248