Allele Selective Antisense Oligonucleotides for Reducing Mutant Huntingtin

Zhong, Z; Brown, JM; Frank-Kamenetsky, M; Aklilu, K; Dodart, JC; Berkovitch, S; Taborn, K; Byrne, M; Iwamoto, N; Vargeese, C

NEUROLOGY, 2019; 92 (15):