Non-Invasively Silencing and Monitoring Machado-Joseph Disease

Nobre, R; Saraiva, J; Fusco, C; Paixao, S; Santana, M; Petrella, L; Sereno, J; Castelhano, J; Castelo-Branco, M; Sena-Esteves, M; de Almeida, LP

MOLECULAR THERAPY, 2018; 26 (5): 269