Phase 1/2 Study of Lumasiran for Treatment of Primary Hyperoxaluria Type 1 A Placebo-Controlled Randomized Clinical Trial

Frishberg, Y; Deschenes, G; Groothoff, JW; Hulton, SA; Magen, D; Harambat, J; van't Hoff, WG; Lorch, U; Milliner, DS; Lieske, JC; Haslett, P; Garg, PP; Vaishnaw, AK; Talamudupula, S; Lu, JD; Habtemariam, BA; Erbe, DV; McGregor, TL; Cochat, P

Frishberg, Y (corresponding author), Shaare Zedek Med Ctr, Div Pediat Nephrol, POB 3235, IL-9103102 Jerusalem, Israel.

CLINICAL JOURNAL OF THE AMERICAN SOCIETY OF NEPHROLOGY, 2021; 16 (7): 1025