Modeling Benefits, Costs, and Affordability of a Novel Gene Therapy in Hemophilia A

ten Ham, RMT; Walker, SM; Soares, MO; Frederix, GWJ; Leebeek, FWG; Fischer, K; Coppens, M; Palmer, SJ

ten Ham, RMT (通讯作者),Utrecht Inst Pharmaceut Sci UIPS, Div Pharmacoepidemiol & Clin Pharmacol, Utrecht, Netherlands.;ten Ham, RMT (通讯作者),Univ York, Ctr Hlth Econ, York, N Yorkshire, England.;ten Ham, RMT (通讯作者),Univ Utrecht, Univ Med Ctr Utrecht, Julius Ctr Hlth Sci & Primary Care, Utrecht, Netherlands.

HEMASPHERE, 2022; 6 (2):

Abstract

The objective was to undertake an early cost-effectiveness assessment of valoctocogene roxaparvovec (valrox; Roctavian) compared to factor (F)VIII pro......

Full Text Link