Safety update: Risdiplam clinical trial development program

Chiriboga, C; Servais, L; Baranello, G; Darras, B; Day, J; Deconinck, N; Farrar, M; Finkel, R; Bertini, E; Kirschner, J; Masson, R; Mazurkiewicz-Beldzinska, M; Vlodavets, D; Bader-Weder, S; Gorni, K; Jaber, B; McIver, T; Papp, G; Scalco, R; Mercuri, E

NEUROMUSCULAR DISORDERS, 2022; 32 (): S89