RNA-based therapies for genodermatoses

Bornert, O; Peking, P; Bremer, J; Koller, U; van den Akker, PC; Aartsma-Rus, A; Pasmooij, AMG; Murauer, EM; Nystrom, A

Nystrom, A (reprint author), Univ Freiburg, Med Ctr, Dept Dermatol, Freiburg, Germany.

EXPERIMENTAL DERMATOLOGY, 2017; 26 (1): 3

Abstract

Genetic disorders affecting the skin, genodermatoses, constitute a large and heterogeneous group of diseases, for which treatment is generally limited......

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