Therapeutic developments for Duchenne muscular dystrophy

Verhaart, IEC; Aartsma-Rus, A

Aartsma-Rus, A (reprint author), Leiden Univ, Med Ctr, Dept Human Genet, Leiden, Netherlands.

NATURE REVIEWS NEUROLOGY, 2019; 15 (7): 373

Abstract

Duchenne muscular dystrophy (DMD) is caused by the lack of functional dystrophin protein. Improvements in patient care and disease management have slo......

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