Correcting CFTR: New Gene Editing Strategies for Rescuing CFTR Function Ex Vivo

Ryan, AL

Ryan, AL (corresponding author), Univ Southern Calif, Dept Med, Div Pulm Crit Care & Sleep Med, Hastings Ctr Pulm Res, Los Angeles, CA 90007 USA.; Ryan, AL (corresponding author), Univ Southern Calif, Dept Stem Cell Biol & Regenerat Med, Los Angeles, CA 90007 USA.

CELL STEM CELL, 2020; 26 (4): 476

Abstract

Gene correction presents one of few options for a cure for all patients with cystic fibrosis. This commentary discusses new applications of CRISPR-bas......

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