Delivery of an Artificial Transcription Factor for Angelman Syndrome Using AAV-PHP.B, AAV-PHP.eB and AAV-DJ/8J with Focused Ultrasound

Beitnere, U; Pyles, B; O'Geen, H; Foiret, J; Zhang, H; Fite, BZ; Ilovitch, T; Mahakian, L; Tam, S; Ferrara, KW; Segal, DJ

MOLECULAR THERAPY, 2018; 26 (5): 140