Sialidase NEU3 action on GM1 ganglioside is neuroprotective in GM1 gangliosidosis

Allende, ML; Lee, YT; Byrnes, C; Li, CL; Tuymetova, G; Bakir, JY; Nicoli, ER; James, VK; Brodbelt, JS; Tifft, CJ; Proia, RL

Proia, RL (通讯作者),Natl Inst Diabet & Digest & Kidney Dis, Genet Dev & Dis Sect, Genet & Biochem Branch, Bethesda, MD 20892 USA.;Tifft, CJ (通讯作者),NIH, Natl Human Genome Res Inst, Med Genet Branch, Bethesda, MD 20894 USA.

JOURNAL OF LIPID RESEARCH, 2023; 64 (12):