Predictive factors for lumacaftor/ivacaftor clinical response

Masson, A; Schneider-Futschik, EK; Baatallah, N; Thao, NK; Girodon, E; Hatton, A; Flament, T; Le Bourgeois, M; Chedevergne, F; Bailly, C; Kyrilli, S; Achimastos, D; Hinzpeter, A; Edelman, A; Sermet-Gaudelus, I

Sermet-Gaudelus, I (reprint author), Inst Necker Enfants Malad, Ctr Reference Malad Rare Mucoviscidose, 149 Rue Sevres, F-75015 Paris, France.

JOURNAL OF CYSTIC FIBROSIS, 2019; 18 (3): 368

Abstract

Background: Ivacaftor-lumacaftor combination therapy corrects the F508 del-CFTR mutated protein which causes Cystic Fibrosis. The clinical response of......

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