Personalized medicine in CF: from modulator development to therapy for cystic fibrosis patients with rare CFTR mutations

Harutyunyan, M; Huang, YJ; Mun, KS; Yang, FMY; Arora, K; Naren, AP

Naren, AP (reprint author), Cincinnati Childrens Hosp Med Ctr, Dept Pediat, Div Pulm Med, 3333 Burnet Ave, Cincinnati, OH 45209 USA.

AMERICAN JOURNAL OF PHYSIOLOGY-LUNG CELLULAR AND MOLECULAR PHYSIOLOGY, 2018; 314 (4): 1529

Abstract

Cystic fibrosis (CF) is the most common life-shortening genetic disease affecting similar to 1 in 3,500 of the Caucasian population. CF is caused by m......

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