Access to Affordable Orphan Medicines in Europe: An EHA Position Paper

Merlini, G; Gribben, J; Macintyre, E; Piggin, M; Doeswijk, R

Merlini, G (corresponding author), Univ Pavia, Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy.

HEMASPHERE, 2020; 4 (5):