Mini-COMET: Safety and efficacy of >= 97 weeks' avalglucosidase alfa in infantile-onset Pompe disease participants previously treated with alglucosidase alfa-MedSci.cn

Mini-COMET: Safety and efficacy of >= 97 weeks' avalglucosidase alfa in infantile-onset Pompe disease participants previously treated with alglucosidase alfa

Kronn, D; Davison, J; Brassier, A; Broomfield, A; Hahn, SH; Kumada, S; Labarthe, F; Ohki, H; Prakalapakorn, SG; Haack, KA; Meng, XZ; Sparks, S; Tammireddy, S; Wilson, C; Zaher, A; Zhou, TY; Chien, YH; Kishnani, P

GENETICS IN MEDICINE, 2022; 24 (3): S348

科室
- - 订阅+
  - 更多科室
工具
服务