Odevixibat therapy in patients with MYO5B mutations: a retrospective case series

Roquelaure, B; Sciveres, M; Grammatikopoulos, T; Lurz, E; Freudenberg, F; Thevathasan, L; Elaraki, F; Valcheva, V; Gonzalès, E

JOURNAL OF HEPATOLOGY, 2023; 78 (): S1002