Nusinersen: First Global Approval

Hoy, SM

Hoy, SM (reprint author), Springer, Private Bag 65901, Auckland 0754, New Zealand.

DRUGS, 2017; 77 (4): 473

Abstract

Spinal muscular atrophy (SMA) is a rare autosomal recessive disorder characterized by muscle atrophy and weakness resulting from motor neuron degenera......

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