Manufacturing challenges and rational formulation development for AAV viral vectors

Srivastava, A; Mallela, KMG; Deorkar, N; Brophy, G

Srivastava, A (corresponding author), Avantor Inc, Biopharma Prod, 1013,US Highway 202-206, Bridgewater, NJ 20220 USA.; Mallela, KMG (corresponding author), Univ Colorado Anschutz Med Campus, Skaggs Sch Pharm & Pharmaceut Sci, Dept Pharmaceut Sci, Ctr Pharmaceut Biotechnol, 12850 East Montview Blvd,MS C238-V20, Aurora, CO 80045 USA.

JOURNAL OF PHARMACEUTICAL SCIENCES, 2021; 110 (7): 2609

Abstract

Adeno-associated virus (AAV) has emerged as a leading platform for gene delivery for treating various diseases due to its excellent safety profile and......

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