Olipudase Alfa in Non-CNS Manifestations of Acid Sphingomyelinase Deficiency: A Profile of Its Use

Syed, YY

Syed, YY (通讯作者),Springer Nat, Private Bag 65901,Mairangi Bay, Auckland 0754, New Zealand.

CLINICAL DRUG INVESTIGATION, 2023; 43 (5): 369