CRISPR-Based Tools for Fighting Rare Diseases

Li, QY; Gao, YM; Wang, HF

Wang, HF (通讯作者),Tsinghua Univ, Tsinghua Peking Ctr Life Sci, Sch Life Sci, Beijing 100084, Peoples R China.;Wang, HF (通讯作者),Tsinghua Univ, Ctr Synthet & Syst Biol, Beijing 100084, Peoples R China.

LIFE-BASEL, 2022; 12 (12):

Abstract

Rare diseases affect the life of a tremendous number of people globally. The CRISPR-Cas system emerged as a powerful genome engineering tool and has f......

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