Volanesorsen and Triglyceride Levels in Familial Chylomicronemia Syndrome

Witztum, JL; Gaudet, D; Freedman, SD; Alexander, VJ; Digenio, A; Williams, KR; Yang, Q; Hughes, SG; Geary, RS; Arca, M; Stroes, ESG; Bergeron, J; Soran, H; Civeira, F; Hemphill, L; Tsimikas, S; Blom, DJ; O'Dea, L; Bruckert, E

Witztum, JL (reprint author), Univ Calif San Diego, Dept Med, M0682,9500 Gilman Dr, La Jolla, CA 92093 USA.; Gaudet, D (reprint author), Univ Montreal, Dept Med, ECOGENE 21 Clin Res Ctr, 225 St Vallier, Chicoutimi, PQ G7H 7P2, Canada.

NEW ENGLAND JOURNAL OF MEDICINE, 2019; 381 (6): 531

Abstract

Background Familial chylomicronemia syndrome is a rare genetic disorder that is caused by loss of lipoprotein lipase activity and characterized by chy......

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