Strategy to detect pre-existing immunity to AAV gene therapy

Falese, L; Sandza, K; Yates, B; Triffault, S; Gangar, S; Long, B; Tsuruda, L; Carter, B; Vettermann, C; Zoog, SJ; Fong, S

Fong, S (reprint author), BioMarin Pharmaceut Inc, Translat Biol, 105 Digital Dr, Novato, CA 94949 USA.

GENE THERAPY, 2017; 24 (12): 768

Abstract

Gene therapy may offer a new treatment option, particularly for patients with severe hemophilia, based on recent research. However, individuals with p......

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