Treatment Potential for LCA5-Associated Leber Congenital Amaurosis

Uyhazi, KE; Aravand, P; Bell, BA; Wei, ZY; Leo, L; Serrano, LW; Pearson, DJ; Shpylchak, I; Pham, J; Vasireddy, V; Bennett, J; Aleman, TS

Aleman, TS (corresponding author), Univ Penn, Perelman Ctr Adv Med, 3400 Civ Ctr Blvd, Philadelphia, PA 19104 USA.

INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2020; 61 (5):

Abstract

PURPOSE. To determine the therapeutic window for gene augmentation for Leber congenital amaurosis (LCA) associated with mutations in LCA5. METHODS. Fi......

Full Text Link


Links

期刊讨论 | 中国SCI论文 | 期刊主页 | 投稿经验 | 杂志官网 | 投稿链接 | 作者需知 | PMC链接 | Pubmed全文检索