Valoctocogene Roxaparvovec and Etranacogene Dezaparavovec: Novel Gene Therapies for Hemophilia A and B

Dougherty, JA; Dougherty, KM

Dougherty, JA (通讯作者),Palm Beach Atlantic Univ, Lloyd L Gregory Sch Pharm, 1301 South Olive Ave, W Palm Beach, FL 33401 USA.

ANNALS OF PHARMACOTHERAPY, 2023; ():

Abstract

Objective: To review efficacy and safety data of valoctocogene roxaparvovec (Roctavian) and etranacogene dezaparavovec (Hemgenix), novel gene therapie......

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