AAV Gene Therapy Prevents and Reverses Heart Failure in a Murine Knockout Model of Barth Syndrome

Wang, SY; Li, YF; Xu, Y; Ma, Q; Lin, ZQ; Schlame, M; Bezzerides, VJ; Strathdee, D; Pu, WLT

Pu, WLT (corresponding author), Boston Childrens Hosp, Dept Cardiol, 300 Longwood Ave, Boston, MA 02115 USA.

CIRCULATION RESEARCH, 2020; 126 (8): 1024