AAV-CRISPR Gene Editing is Negated by Pre-Existing Immunity to Cas9

Li, A; Lee, CM; Tanner, MR; Hurley, AE; De Giorgi, M; Jarrett, KE; Davis, TH; Doerfler, AM; Bao, G; Beeton, C; Lagor, WR

MOLECULAR THERAPY, 2020; 28 (4): 565