Arginase I mRNA therapy - a novel approach to rescue arginase 1 enzyme deficiency

Asrani, KH; Cheng, L; Cheng, CJ; Subramanian, RR

Subramanian, RR (reprint author), Alexion Pharmaceut Inc, Discovery Res Cambridge, Cambridge, MA 02139 USA.

RNA BIOLOGY, 2018; 15 (7): 914