AAV-mediated protein trans-splicing in the retina

Tornabene, P; Trapani, I; Toriello, E; Minopoli, R; Centrulo, M; Lupo, M; de Simone, S; Tiberi, P; Dell'Aquila, F; Iodice, C; Albert, S; Hoyng, CB; Cremers, FPM; Gesualdo, C; Simonelli, F; Auricchio, A

HUMAN GENE THERAPY, 2018; 29 (12): A80