Whole-blood transcriptomic responses to lumacaftor/ivacaftor therapy in cystic fibrosis

Kopp, BT; Fitch, J; Jaramillo, L; Shrestha, CL; Robledo-Avila, F; Zhang, SZ; Palacios, S; Woodley, F; Hayes, D; Partida-Sanchez, S; Ramilo, O; White, P; Mejias, A

Kopp, BT (corresponding author), Nationwide Childrens Hosp, W510,700 Childrens Dr, Columbus, OH 43205 USA.

JOURNAL OF CYSTIC FIBROSIS, 2020; 19 (2): 245

Abstract

Background: Cystic fibrosis (CF) remains without a definitive cure. Novel therapeutics targeting the causative defect in the cystic fibrosis transmemb......

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