Muscle-Specific Promoters for Gene Therapy

Skopenkova, VV; Egorova, TV; Bardina, MV

Skopenkova, VV (corresponding author), Russian Acad Sci, Inst Gene Biol, Moscow 119334, Russia.; Skopenkova, VV (corresponding author), Marlin Biotech LLC, Moscow 121205, Russia.; Skopenkova, VV (corresponding author), Russian Acad Sci, Inst Gene Biol, Ctr Precis Genome Editing & Genet Technol Biomed, Moscow 119334, Russia.

ACTA NATURAE, 2021; 13 (1): 47

Abstract

Many genetic diseases that are responsible for muscular disorders have been described to date. Gene replacement therapy is a state-of-the-art strategy......

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