Redirecting AAV vectors to extrahepatic tissues

Asokan, A; Shen, S

Asokan, A (通讯作者),Duke Univ, Sch Med, Dept Surg, Durham, NC 27707 USA.;Shen, S (通讯作者),Vertex Pharmaceut, 50 Northern Ave, Boston, MA 02210 USA.

MOLECULAR THERAPY, 2023; 31 (12): 3371

Abstract

Recombinant adeno-associated viral (AAV) vectors are the current benchmark for systemic delivery of gene therapies to multiple organs in vivo. Despite......

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