Durable Recovery of Auditory Function Following Intracochlear Delivery of AK-OTOF (AAVAnc80-hOTOF Vector) in a Translationally Relevant Mouse Model of Otoferlin Gene (OTOF)-Mediated Hearing Loss

Hickox, AE; Gao, Y; Yu, FF; Darcy, Y; Reape, K; Francis, SP; Kim, YH; Davis, S; Schamber, P; Syed, J; Gribble, KD; Qu, EP; Churchill, RM; Andres-Mateos, E; Wellman, JA; Valero, MD

MOLECULAR THERAPY, 2021; 29 (4): 276